Resources for healthcare professionals
Guide to reconstitution and administration
This resource has been developed to help healthcare professionals with the dosing, reconstitution and administration of Pombiliti® and Opfolda®.
Guide to starting a patient on treatment
Treatment day checklist and frequently asked questions for healthcare professionals
This resource has been developed to support healthcare professionals with common questions around the reconstitution, dosing and administration of Pombiliti® and Opfolda® when initiating a patient on treatment.
Physical function monitoring in LOPD
This video explores key assessments and tools that can be used to monitor the physical functioning of patients with late-onset Pompe disease (LOPD).
NSAD demonstration
This video aims to teach healthcare professionals about the North Star Assessment for Limb Girdle Type Muscular Dystrophies (NSAD), including what the assessment tool contains and how it should be performed.
R-Pact scale and other PRO measures in LOPD
In this video, discover how patient-reported outcome (PRO) measures, including the R-Pact scale, can provide insight into the lived experience of people with late-onset Pompe disease (LOPD), helping healthcare professionals understand the impact of the disease on their daily lives.
Respiratory monitoring using SNIP versus other methods in LOPD
This video delves into the use of sniff nasal inspiratory pressure (SNIP) as a respiratory monitoring tool in late-onset Pompe disease (LOPD), comparing its benefits and utility with those of other monitoring tools.
